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Vol. I · No. 40 Texas Edition
Sunday, Nov 8
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How one family gave a critical boost to gene therapy research

By Sydney Lupkin 3 views 0 comments
How one family gave a critical boost to gene therapy research
Image: NPR

A family affected by Sanfilippo syndrome raised millions of dollars for research. The Food and Drug Administration just approved a gene therapy the support helped make possible.

NPR Original story · www.npr.org
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